Conference Day One

Conference Day One | Wednesday, December 11, 2024

7:20 am Morning Registration & Coffee

8:20 am Chair’s Opening Remarks

  • Michael Holers Professor - Medicine, University of Colorado Denver | Anschutz Medical Campus

Advancing Complement Therapies: Pathways, Clinical Insights & Future Directions

8:30 am Panel Discussion: Dysregulation Insights: An Overview of the Complement System in Health & Human Disease

Synopsis

  • Unravelling the 3 complement pathways and potential intervention points
  • Understanding core processes in healthy inflammatory response in comparison to pathophysiology of autoimmune conditions
  • Discussing the optimal modalities for delivering complement mediated drugs: small molecules, antibodies, and gene therapies

9:00 am The Role of Haem in the Complement System

  • Karina Yazdanbakhsh Vice President & Head of Complement Bio Laboratory, New York Blood Center

Synopsis

Haem-binding proteins in regulating complement activation

Pathophysiological mechanisms underlying haem-induced tissue damage

Development of haem-binding proteins or complement inhibitors to prevent haem-mediated complement activation

9:30 am Reserved for Machaon Diagnostics

9:45 am Complement Combinations: Exploring Potential of Complement Inhibitor Combinations in Patients with PNH

  • Deepak Jain Vice President, Global Program Team Leader, Alexion Pharmaceuticals

Synopsis

  • Importance of sustained control of terminal complement activity to prevent the most severe consequences of PNH
  • Role of proximal complement inhibition without compromising terminal complement inhibition in patients with PNH

10:15 am Targeting Complement C3 and Factor B with siRNA: Concept to Clinic

  • James Hamilton Chief of Discovery & Translational Medicine, Arrowhead Pharmaceuticals Inc.

Synopsis

  • Lessons learned from discovery and early preclinical complement inhibitor studies
  • Using Complement Factor B inhibitors to target the alternative pathway
  • Evaluating safety, tolerability, PK/PD in C3 and Factor B inhibitors to treat renal disease

10:45 am Speed Networking

Synopsis

This informal session provides the perfect opportunity to connect with the industry frontrunners and key opinion leaders in the complement targeting field. Establish meaningful connections to build upon for the rest of the conference and gain exclusive first-hand insights into the latest research and developments driving progress in modulating, inhibiting and activating the complement system.

11:15 am Morning Break

Optimizing Complement Targeting Strategies: Acute vs. Chronic Inflammation & Homeostasis

11:45 am Panel Discussion: Upstream, Downstream or Proximal – Where, When, & How to Target?

Synopsis

  • Discussing acute versus chronic inflammatory disorders and which proteins within the cascade we can target
  • Understanding disease progression and debating systemic or tissue specific targeting
  • Can combination therapies bridge the gaps and ensure efficacy for treatment?

12:15 pm Reserved for National Jewish Health

Synopsis

National Jewish Health | VuMedi

12:30 pm GBS vs. GA: Treating Both Acute & Chronic Diseases with C1q Inhibition

Synopsis

  • Discussing the efficacy of ANX005 in treating Guillain-Barre Syndrome
  • Optimizing dosage for acute and chronic indications
  • Summarizing the differences in the challenges of complement inhibition in acute and chronic indications

1:00 pm Lunch Break

Recent Advancements & Exploring When to Pursue RNAi & Gene Therapies

2:00 pm Ligand & Enhancer Assisted Delivery for RNAi Complement Inhibitors

  • Shiyu Wang Co-Founder & Chief Scientific Officer, SanegeneBio

Synopsis

  • Targeting C3 with siRNA
  • Delivering a GalNAc conjugate to the liver using the LEAD GalNac platform
  • Discussing optimal dosage for long-term efficacy

3:00 pm RNAi Therapeutics Coming of Age: Targeting Complement Genes to Treat Rheumatoid Arthritis

  • Nirmal Banda professor, University of Colorado Anschutz Medical Campus

Synopsis

  • siRNAs to target the “undruggable” candidates and how these fit within the complement cascade
  • Considering tissue specific targeting to ensure healthy complement activity remains
  • Clinical data updated for the use of siRNA-based complement inhibitors in Rheumatoid Arthritis

3:30 pm Afternoon Break & Poster Session

Synopsis

Immerse yourself in an engaging and informal session, join your peers in a relaxed atmosphere that encourages meaningful conversations and discussions. Explore a range of exciting poster presentations and showcase your own developments in the Complement-Based Drug Development world. Don’t miss out on the chance to submit your own posters and get ready to connect, learn, and present. To submit your poster please contact info@hansonwade.com.

4:00 pm Preclinical Updates for Complement Regulators Using Gene Therapies

Synopsis

  • The benefits of using gene therapies to target complement mediated diseases
  • Using a localised approach to target the eye and mitigate toxicity
  • Updates in targeting Geographic Atrophy/Dry AMD

4:30 pm Roundtable Discussion: Assays, Biomarkers & Computational Modelling in Complement Inhibitor Development

Synopsis

This interactive session gives you the opportunity to be part of the discussion, share ideas and learn from your peers. Choose the table most relevant to you, and get ready to be part of this conversation. Topics to consider:

Improving Reliability &
Making Informed Assay
Choices for Complement
Based Drugs

Validating Qualitative &
Developing Quantitative
Biomarkers for
Complement

Mimicking Mechanistic
Understanding
through Computational
Modelling

Closing this session with an audience wide discussion on enhancing assay reliability, biomarker validation, and computational modelling in complement-based drug development to better standardize comparison of results across the field.

5:00 pm Chair’s Closing Remarks

  • Michael Holers Professor - Medicine, University of Colorado Denver | Anschutz Medical Campus

5:10 pm End of Conference Day One